Gene therapy injection into spinal cord halts ALS in adult mice

Written by Chelsea Whyte
A new delivery method could take us a step closer to a gene therapy for amyotrophic lateral sclerosis (ALS), a neurodegenerative disorder in which nerve cells progressively stop working throughout the spinal cord and the brain.
Animal studies have already suggested that ALS can be prevented by replacing the mutated genes that cause some forms of the condition with normal versions. But delivering genes to nerve cells in the spine is a challenge. Read more.